Related Experiment Video

Updated: Aug 8, 2026

A Standard Methodology to Examine On-site Mutagenicity As a Function of Point Mutation Repair Catalyzed by CRISPR/Cas9 and SsODN in Human Cells
10:07

A Standard Methodology to Examine On-site Mutagenicity As a Function of Point Mutation Repair Catalyzed by CRISPR/Cas9 and SsODN in Human Cells

Published on: August 25, 2017

Some Aim to Fix the Genes Themselves

Waldholz1

  • 1The Wall Street Journal, New York, New York, USA.

The Oncologist
|July 1, 1999
PubMed

Insights

Gene therapy shows promise in halting cancer growth by repairing defective genes. This innovative approach may be available to patients within two years, offering new hope for cancer treatment.

Area of Science:

  • Oncology
  • Genetics
  • Biotechnology

Background:

  • Cancer is understood as a disease caused by genetic mutations.
  • The concept of correcting these genetic defects to treat cancer has been a long-standing goal in medical research.

Purpose of the Study:

  • To present the initial findings of a novel gene therapy technique aimed at stalling tumor growth.
  • To evaluate the efficacy of repairing damaged genes in patients with advanced cancer.

Main Methods:

  • The study involves "cancer gene therapy," an innovative method for repairing damaged genes.
  • Initial trials were conducted on approximately one hundred severely ill patients.

Main Results:

  • Early results indicate that cancer growth can be stalled in patients undergoing this gene therapy.
  • The findings represent a significant step forward in demonstrating the potential of gene repair for cancer treatment.

Conclusions:

  • Cancer gene therapy shows potential for stalling tumor progression in severely ill patients.
  • If further studies confirm these results, the technique could be clinically available in approximately two years.

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