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A Target-Specific Cellular Assay for Screening of Topoisomerase I Inhibitors

Spaltmann1, Lohrmann, Ziegelbauer

  • 1Bayer AG, Institut für Antiinfektiva Forschung, Wuppertal, Germany.

Insights

A new high-throughput assay using Saccharomyces cerevisiae detects topoisomerase I inhibitors. This method significantly reduces the number of compounds needing retesting by over 90%.

Area of Science:

  • Biochemistry and Molecular Biology
  • Drug Discovery and Development
  • Yeast Genetics and Cell Biology

Background:

  • Topoisomerase I is a key enzyme in DNA topology regulation, targeted by anticancer drugs and a potential target for antifungal agents.
  • Existing methods for identifying topoisomerase I inhibitors can be labor-intensive and may yield a high number of false positives.

Purpose of the Study:

  • To develop a cellular, target-specific high-throughput assay for identifying topoisomerase I inhibitors.
  • To utilize a Saccharomyces cerevisiae (yeast) system with differentially labeled wild-type and topoisomerase I deletion mutant strains for efficient screening.

Main Methods:

  • Development of a dual-strain yeast assay using wild-type and DeltatopI (topoisomerase I deletion mutant) Saccharomyces cerevisiae strains, each labeled with a distinct green fluorescent protein (GFP) variant.
  • Independent quantification of the growth of both yeast strains when mixed and exposed to various compounds.
  • Screening of compound libraries to identify inhibitors specifically targeting topoisomerase I.

Main Results:

  • The assay successfully differentiated between topoisomerase I-specific inhibitors (e.g., camptothecin, inhibiting only the wild-type strain) and broad-spectrum agents (e.g., amphotericin B, inhibiting both strains).
  • Only 0.06% of screened compounds inhibited the wild-type strain but not the DeltatopI strain, compared to 0.9% inhibiting both.
  • The DeltatopI strain as an internal control reduced the number of candidate topoisomerase I inhibitors requiring retesting by over 90%.

Conclusions:

  • The developed Saccharomyces cerevisiae-based cellular high-throughput assay is highly effective for specific detection of topoisomerase I inhibitors.
  • This assay significantly enhances screening efficiency by minimizing false positives and reducing the workload for subsequent validation steps.
  • The methodology offers a robust platform for discovering novel anticancer and antifungal agents targeting topoisomerase I.

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