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Vitamin D deficiency and disorders of vitamin D metabolism

M K Thomas1, M B Demay

  • 1Department of Medicine, Harvard Medical School, Boston, Massachusetts, USA.

Insights

Inherited vitamin D metabolism disorders, though rare, reveal vitamin D's crucial roles. Widespread vitamin D deficiency, especially in the elderly, necessitates broader screening beyond known risk factors.

Area of Science:

  • Endocrinology
  • Metabolic disorders
  • Molecular genetics

Background:

  • Disorders of vitamin D metabolism stem from inherited mutations affecting the vitamin D receptor or key metabolic enzymes.
  • These genetic defects disrupt the conversion of vitamin D to its active form, 1,25-dihydroxyvitamin D.
  • Research in affected individuals and animal models has elucidated vitamin D's critical functions and mechanisms of action.

Purpose of the Study:

  • To summarize the understanding of inherited vitamin D metabolism disorders.
  • To highlight the growing prevalence of vitamin D deficiency in the general population, particularly among the elderly.
  • To advocate for expanded screening protocols for vitamin D deficiency.

Main Methods:

  • Review of studies on patients with inherited vitamin D metabolism disorders.
  • Analysis of data from animal models of vitamin D metabolism defects.
  • Epidemiological data on vitamin D deficiency prevalence.

Main Results:

  • Mutations in vitamin D metabolism pathways, while rare, provide insights into vitamin D's biological significance.
  • Vitamin D deficiency is a common and increasing health concern across various demographics.
  • Current screening practices, limited to high-risk individuals, miss a substantial number of deficient patients.

Conclusions:

  • Understanding rare genetic disorders enhances knowledge of vitamin D's physiological importance.
  • Vitamin D deficiency represents a significant public health issue requiring attention.
  • Broadening screening criteria for vitamin D deficiency is essential for effective diagnosis and management.

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