Related Experiment Videos
The potential for therapy of immune disorders with gene therapy
1Disorders of Immunity Section, Clinical Gene Therapy Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA.
Pediatric Clinics of North America
|December 29, 2000
Abstract:
Several hurdles remain before gene therapy will be a part of mainstream medical therapy; however, the preliminary report of success in HSC correction in patients with XSCID provides hope that gene therapy will become a reality.