Comparative evaluation of the antitumor activity of antiangiogenic proteins delivered by gene transfer
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Published on: December 1, 2013
1Department of Genetics, Harvard Medical School, Division of Molecular Medicine, Children's Hospital, Boston, MA 02115, USA.
Abstract:
Although the systemic administration of a number of different gene products has been shown to result in the inhibition of angiogenesis and tumor growth in different animal tumor models, the relative potency of those gene products has not been studied rigorously. To address this issue, recombinant adenoviruses encoding angiostatin, endostatin, and the ligand-binding ectodomains of the vascular endothelial growth factor receptors Flk1, Flt1, and neuropilin were generated and used to systemically deliver the different gene products in several different preexisting murine tumor models. Single i.v. injections of viruses encoding soluble forms of Flk1 or Flt1 resulted in approximately 80% inhibition of preexisting tumor growth in murine models involving both murine (Lewis lung carcinoma, T241 fibrosarcoma) and human (BxPC3 pancreatic carcinoma) tumors. In contrast, adenoviruses encoding angiostatin, endostatin, or neuropilin were significantly less effective. A strong correlation was observed between the effects of the different viruses on tumor growth and the activity of the viruses in the inhibition of corneal micropocket angiogenesis. These data underscore the need for comparative analyses of different therapeutic approaches that target tumor angiogenesis and provide a rationale for the selection of specific antiangiogenic gene products as lead candidates for use in gene therapy approaches aimed at the treatment of malignant and ocular disorders.
Insights
Gene therapy using soluble vascular endothelial growth factor receptors (Flk1, Flt1) effectively inhibited tumor growth and angiogenesis. Other gene products like angiostatin were less potent, highlighting the need for comparative analysis in gene therapy development.
Area of Science:
- Oncology
- Gene Therapy
- Molecular Biology
Background:
- Systemic gene product administration can inhibit tumor growth and angiogenesis.
- The relative efficacy of different anti-angiogenic gene products requires rigorous comparison.
Purpose of the Study:
- To compare the potency of various gene products in inhibiting tumor growth and angiogenesis.
- To identify lead gene therapy candidates for malignant and ocular disorders.
Main Methods:
- Generated recombinant adenoviruses encoding angiostatin, endostatin, soluble Flk1, soluble Flt1, and neuropilin.
- Administered gene products systemically via single intravenous injections into established murine tumor models.
- Assessed tumor growth inhibition and corneal micropocket angiogenesis inhibition.
Main Results:
- Soluble Flk1 and Flt1 gene products achieved approximately 80% inhibition of tumor growth in murine and human tumor models.
- Adenoviruses encoding angiostatin, endostatin, or neuropilin demonstrated significantly less efficacy.
- Strong correlation observed between tumor growth inhibition and anti-angiogenic activity in corneal assays.
Conclusions:
- Soluble vascular endothelial growth factor receptor gene products are potent inhibitors of tumor angiogenesis and growth.
- Comparative analysis is crucial for selecting effective anti-angiogenic gene therapy candidates.
- Flk1 and Flt1 represent promising lead candidates for gene therapy in cancer and ocular diseases.

