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Published on: August 6, 2014
Tg.AC genetically altered mouse: assay working group overview of available data
W C Eastin1, J H Mennear, R W Tennant
1National Institute of Environmental Health Sciences, National Toxicology Program, Research Triangle Park, North Carolina 27713-2233, USA. eastin@niehs.nih.gov
Abstract:
In a Government/Industry/Academic partnership to evaluate alternative approaches to carcinogenicity testing, 21 pharmaceutical agents representing a variety of chemical and pharmacological classes and possessing known human and or rodent carcinogenic potential were selected for study in several rodent models. The studies from this partnership project, coordinated by the International Life Sciences Institute, provide additional data to better understand the models' limitations and sensitivity in identifying carcinogens. The results of these alternative model studies were reviewed by members of Assay Working Groups (AWG) composed of scientists from government and industry with expertise in toxicology, genetics, statistics, and pathology. The Tg.AC genetically manipulated mouse was one of the models selected for this project based on previous studies indicating that Tg.AC mice seem to respond to topical application of either mutagenic or nonmutagenic carcinogens with papilloma formation at the site of application. This communication describes the results and AWG interpretations of studies conducted on 14 chemicals administered by the topical and oral (gavage and/or diet) routes to Tg.AC genetically manipulated mice. Cyclosporin A, an immunosuppresant human carcinogen, ethinyl estradiol and diethylstilbestrol (human hormone carcinogens) and clofibrate, an hepatocarcinogenic peroxisome proliferator in rodents, were considered clearly positive in the topical studies. In the oral studies, ethinyl estradiol and diethylstilbestrol were negative, cyclosporin was considered equivocal, and results were not available for the clofibrate study. Of the 3 genotoxic human carcinogens (phenacetin, melphalan, and cyclophosphamide), phenacetin was negative by both the topical and oral routes. Melphalan and cyclophosphamide are, respectively, direct and indirect DNA alkylating agents and topical administration of both caused equivocal responses. With the exception of clofibrate, Tg.AC mice did not exhibit tumor responses to the rodent carcinogens that were putative human noncarcinogens, (di(2-ethylhexyl) phthalate, methapyraline HCl, phenobarbital Na, reserpine, sulfamethoxazole or WY-14643, or the nongenotoxic, noncarcinogen, sulfisoxazole) regardless of route of administration. Based on the observed responses in these studies, it was concluded by the AWG that the Tg.AC model was not overly sensitive and possesses utility as an adjunct to the battery of toxicity studies used to establish human carcinogenic risk.
Insights
The Tg.AC mouse model showed varied responses to carcinogens, proving useful for identifying potential human carcinogens. This alternative testing approach aids in understanding carcinogenicity and assessing human risk.
Area of Science:
- Toxicology
- Genetics
- Carcinogenicity Testing
Background:
- Pharmaceutical agents with known carcinogenic potential were evaluated using alternative testing models.
- The Tg.AC genetically manipulated mouse model was chosen for its responsiveness to carcinogen application.
- Previous studies suggested Tg.AC mice develop papillomas upon topical carcinogen exposure.
Purpose of the Study:
- To evaluate the utility of the Tg.AC mouse model in carcinogenicity testing.
- To assess the sensitivity and limitations of the Tg.AC model in identifying human and rodent carcinogens.
- To compare Tg.AC mouse responses to topical and oral administration of various chemicals.
Main Methods:
- 14 chemicals were administered to Tg.AC mice via topical and oral routes (gavage and/or diet).
- Chemicals included known human carcinogens (e.g., Cyclosporin A, ethinyl estradiol, diethylstilbestrol) and rodent carcinogens.
- Responses were reviewed by an Assay Working Group (AWG) of toxicology and pathology experts.
Main Results:
- Topical administration showed clear positive responses for Cyclosporin A, ethinyl estradiol, diethylstilbestrol, and clofibrate.
- Oral administration yielded negative results for ethinyl estradiol and diethylstilbestrol, and equivocal for Cyclosporin A.
- Phenacetin was negative for both routes; melphalan and cyclophosphamide showed equivocal topical responses. Most rodent carcinogens did not elicit tumor responses.
Conclusions:
- The Tg.AC mouse model demonstrated utility as an adjunct for carcinogenicity testing.
- The model was not overly sensitive, providing valuable data for human carcinogenic risk assessment.
- Further data is needed to fully understand the model's limitations and sensitivity across different chemical classes and exposure routes.
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