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Vitamin D analogue-specific recruitment of vitamin D receptor coactivators

Laura L Issa1, Gary M Leong, Robert L Sutherland

  • 1Bone and Mineral Program, Garvan Institute of Medical Research, St. Vincent's Hospital, Sydney, NSW, Australia.

Insights

Synthetic vitamin D receptor (VDR) ligands show therapeutic promise. Ligand structure influences VDR

Area of Science:

  • Biochemistry
  • Molecular Biology
  • Endocrinology

Background:

  • Synthetic vitamin D receptor (VDR) ligands offer therapeutic potential for various diseases.
  • Differential actions of VDR ligands, including antiproliferative and hypercalcemic effects, are not fully understood.
  • Selective recruitment of transcriptional coactivators by VDR ligands is hypothesized to mediate gene- and tissue-specific effects.

Purpose of the Study:

  • To investigate how ligand structure influences the interaction between the VDR and its coactivators.
  • To identify structural elements in VDR ligands critical for VDR-coactivator complex formation.
  • To correlate VDR-coactivator interactions with ligand-induced gene transactivation.

Main Methods:

  • Synthesis and assessment of 20-R- and 20-S (20-epi)-modified VDR analogues.
  • Evaluation of VDR's ability to recruit coactivators GRIP1 and RAC3 upon activation by these analogues.
  • Analysis of VDR-coactivator binding affinity and its correlation with ligand-receptor binding.
  • Assessment of coactivator potentiation of analogue-induced transactivation of the osteocalcin gene promoter.

Main Results:

  • VDR-coactivator interaction strength was ligand-specific and did not always correlate with binding affinity.
  • 20-epi analogues generally enhanced VDR-coactivator interactions compared to calcitriol.
  • 20-R analogues were less effective than calcitriol in promoting VDR-coactivator interactions.
  • Specific side-chain modifications (16-ene, 23-yne, fluorinated substituents) attenuated coactivator binding.
  • Enhanced GRIP1 recruitment by 20-epi analogues correlated with potentiated osteocalcin gene promoter activity.

Conclusions:

  • Ligand structure, particularly the side-chain and its orientation, significantly impacts VDR's avidity for coactivator binding.
  • Selective recruitment of coactivators by VDR ligands is a key mechanism underlying their gene- and tissue-specific actions.
  • These findings provide insights into the rational design of VDR-based therapeutics with improved efficacy and reduced side effects.

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