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Engineering Oncogenic Heterozygous Gain-of-Function Mutations in Human Hematopoietic Stem and Progenitor Cells
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Gene therapy for fanconi anemia

James M Croop1

  • 1Pediatric Hematology/Oncology, James Whitcomb Riley Hospital for Children, 702 Barnhill Drive, Indianapolis, IN 46202, USA. jcroop@iupui.edu

Current Hematology Reports
|August 7, 2003
PubMed

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