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Targeted gene repair -- in the arena

Eric B Kmiec1

  • 1Department of Biology, Delaware Biotechnology Institute, University of Delaware, Newark, Delaware 19716, USA. ekmiec@udel.edu

The Journal of Clinical Investigation
|September 4, 2003
PubMed
Summary

Targeted gene repair uses synthetic DNA to correct genetic defects by activating natural repair systems. This promising gene therapy alternative shows potential for treating inherited diseases.

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