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Cost-utility analysis in evaluating prophylaxis in haemophilia

M Carcao1, W J Ungar, B M Feldman

  • 1Department of Paediatrics, Divisions of Haematology/Oncology, Hospital for Sick Children, Toronto, Canada. manuel.carcao@sickkids.ca

Summary

Prophylaxis in haemophilia management, though costly, reduces joint bleeds and damage. Cost-utility analysis (CUA) using quality-adjusted life years (QALYs) helps evaluate its value against other treatments.

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