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Updated: Aug 23, 2026

Evaluation of Exon Inclusion Induced by Splice Switching Antisense Oligonucleotides in SMA Patient Fibroblasts
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Published on: May 11, 2018

In vivo selection reveals combinatorial controls that define a critical exon in the spinal muscular atrophy genes

Natalia N Singh1, Elliot J Androphy, Ravindra N Singh

  • 1Department of Medicine (LRB 326), University of Massachusetts Medical School, 364 Plantation Street, Worcester, MA 01605-2324, USA. Ravindra.Singh@umassmed.edu

RNA (New York, N.Y.)
|July 24, 2004
PubMed

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