Diamond-Blackfan anemia responding to valproic acid

Update of the decision-making algorithm on selecting transfusion-dependent β-thalassemic patients for gene therapy approaches: joint consensus report on behalf of EHA-specialized working group and EBMT hemoglobinopathies working party.

Bone marrow transplantation·2026

EHA Recommendations for preconceptual and antenatal screening and prenatal diagnosis for hemoglobinopathies.

HemaSphere·2026

Phase 2a randomized study to evaluate sapablursen in patients with non-transfusion dependent β-thalassemia intermedia.

Blood advances·2026

How I manage luspatercept in transfusion-dependent beta-thalassemia.

HemaSphere·2026

Spirituality and cancer: quality of life, anxiety/depression and symptom severity.

BMJ supportive & palliative care·2025

Safety and pharmacodynamics of the ferroportin inhibitor vamifeport in patients with non-transfusion-dependent β-thalassemia: results from a randomized phase 2a study.

Orphanet journal of rare diseases·2025

Measurable Residual Disease-Dependent Unfavorable Outcomes in Pediatric PAX5-Rearranged B-Acute Lymphoblastic Leukemia.

Blood·2026

The hepatic FGFR-ERK-HRG axis regulates heparin-induced thrombocytopenia with thrombosis.

Blood·2026

HOW I TREAT BLEEDING IN WOMEN AND GIRLS WITH HEMOPHILIA/ HEMOPHILIA CARRIERS.

Blood·2026

FERMT3 alternative splicing enhances kindlin-3 membrane recruitment for neutrophil adhesion during stress myelopoiesis.

Blood·2026

Risk of recurrence in patients with provoked venous thromboembolism: a prospective cohort study.

Blood·2026

How I treat autoimmune neutropenia in adults.

Blood·2026

Determining aerosol temperatures by oxygen K-edge X-ray thermometry.

Physical chemistry chemical physics : PCCP·2026

Potential Mechanisms of Platelet Dysfunction and Bleeding in Acid Sphingomyelinase Deficiency.

Cells·2026

APOE and genetic risk variants influence Alzheimer's disease onset in carriers of an extra copy of APP, with and without Down syndrome.

Alzheimer's & dementia : the journal of the Alzheimer's Association·2026

Effects of an Alkane on the Adsorption and Collapse by the Lipids of Pulmonary Surfactant.

Biophysical journal·2026

Atmospheres as Habitats.

Astrobiology·2026

Focal Vascular Photopenia as a Metabolic Signature of Pulmonary Embolism on AI-Enhanced 18F-FDG PET/CT.

Clinical nuclear medicine·2026

Related Experiment Videos

Diamond-Blackfan anemia responding to valproic acid

Related Concept Videos

Update of the decision-making algorithm on selecting transfusion-dependent β-thalassemic patients for gene therapy approaches: joint consensus report on behalf of EHA-specialized working group and EBMT hemoglobinopathies working party.

EHA Recommendations for preconceptual and antenatal screening and prenatal diagnosis for hemoglobinopathies.

Phase 2a randomized study to evaluate sapablursen in patients with non-transfusion dependent β-thalassemia intermedia.

How I manage luspatercept in transfusion-dependent beta-thalassemia.

Spirituality and cancer: quality of life, anxiety/depression and symptom severity.

Safety and pharmacodynamics of the ferroportin inhibitor vamifeport in patients with non-transfusion-dependent β-thalassemia: results from a randomized phase 2a study.

Measurable Residual Disease-Dependent Unfavorable Outcomes in Pediatric PAX5-Rearranged B-Acute Lymphoblastic Leukemia.

The hepatic FGFR-ERK-HRG axis regulates heparin-induced thrombocytopenia with thrombosis.

HOW I TREAT BLEEDING IN WOMEN AND GIRLS WITH HEMOPHILIA/ HEMOPHILIA CARRIERS.

FERMT3 alternative splicing enhances kindlin-3 membrane recruitment for neutrophil adhesion during stress myelopoiesis.

Risk of recurrence in patients with provoked venous thromboembolism: a prospective cohort study.

How I treat autoimmune neutropenia in adults.

Determining aerosol temperatures by oxygen K-edge X-ray thermometry.

Potential Mechanisms of Platelet Dysfunction and Bleeding in Acid Sphingomyelinase Deficiency.

APOE and genetic risk variants influence Alzheimer's disease onset in carriers of an extra copy of APP, with and without Down syndrome.

Effects of an Alkane on the Adsorption and Collapse by the Lipids of Pulmonary Surfactant.

Atmospheres as Habitats.

Focal Vascular Photopenia as a Metabolic Signature of Pulmonary Embolism on AI-Enhanced 18F-FDG PET/CT.

Related Experiment Videos

Diamond-Blackfan anemia responding to valproic acid

Related Concept Videos

Related Articles