A single, abbreviated RPGR-ORF15 variant reconstitutes RPGR function in vivo

Dong-Hyun Hong1, Basil S Pawlyk, Michael Adamian

  • 1Berman-Gund Laboratory for the Study of Retinal Degenerations, Harvard Medical School, Massachusetts Eye and Ear Infirmary, Boston, Massachusetts 02114, USA.

Abstract

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