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A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference

Selda Samakoglu1, Leszek Lisowski, Tulin Budak-Alpdogan

  • 1Laboratory of Gene Transfer and Gene Expression, Sloan-Kettering Institute, New York, New York 10021, USA.

Nature Biotechnology
|December 27, 2005
PubMed

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