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Updated: Jun 17, 2026

Generation of Multivirus-specific T Cells to Prevent/treat Viral Infections after Allogeneic Hematopoietic Stem Cell Transplant
08:52

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Gene therapy for severe combined immunodeficiency: are we there yet?

Marina Cavazzana-Calvo1, Alain Fischer

  • 1INSERM U768 and Université Paris Descartes, Paris, France. m.cavazzana@nck.aphp.fr

The Journal of Clinical Investigation
|June 6, 2007
PubMed
Summary

Gene therapy offers a promising alternative for treating hematopoietic diseases when HLA-matched donors are unavailable. This review explores gene-modified autologous transplantation for SCID, addressing safety and efficacy.

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