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CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications
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Pharmacogenomics and therapeutics of hemoglobinopathies

George P Patrinos1, Frank G Grosveld

  • 1Erasmus Medical Center, Faculty of Medicine and Health Sciences Medical Genetics Cluster-Department of Cell Biology and Genetics, Rotterdam, The Netherlands. g.patrinos@erasmusmc.nl

Hemoglobin
|February 16, 2008
PubMed

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