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Related Concept Videos

Gene Therapy00:59

Gene Therapy

Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be inserted. The...

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A "vector drain" in US gene therapy development?

Michel Sadelain, David A Williams

    Molecular Therapy : the Journal of the American Society of Gene Therapy
    |April 25, 2008
    PubMed
    Summary

    No abstract available in PubMed .

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