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Published on: July 23, 2016
Drug delivery systems: application of liposomal anti-tumor agents to neuroectodermal cancer treatment
Daniela Di Paolo1, Fabio Pastorino, Chiara Brignole
1Experimental Therapies Unit, Laboratory of Oncology, G. Gaslini Children's Hospital, Genoa, Italy. danieladipaolo@ospedale-gaslini.ge.it
Abstract:
Disseminated neuroectoderma-derived tumors, mainly neuroblastoma in childhood and melanoma in the adulthood, are refractory to most current therapeutic regimens and hence the prognosis remains very poor. Preclinical research studies have indicated several agents that show promising therapeutic potential for these neoplasms. However, there appears to be a limitation to their in vivo applicability, mainly due to unfavorable pharmacokinetic properties that lead to insufficient drug delivery to the tumor or metastatic sites or to high systemic or organ-specific toxicity. In this scenario, the focus is on targeted cancer therapy. Encapsulating anticancer drugs in liposomes enables targeted drug delivery to tumor tissue and prevents damage to the normal surrounding tissue. Indeed, sterically stabilized liposomes have been shown to enhance the selective localization of entrapped drugs to solid tumors, with improvements in therapeutic indices. The identification of tumor-associated antigens and/or genes and the relative ease of manipulating the physicochemical features of liposome hold promise for the development of novel therapeutic strategies that selectively target tumor cells. Combined targeting is still investigated, especially the availability to simultaneously target and kill both the cancer cells and the tumor vasculature. Animal models make it possible to link molecular genetics and biochemistry information to the physiological basis of disease and are important predictive tools that offer a frontline testing system for studying the involvement of specific genes and the efficacy of novel therapeutics approaches. Relevant experimental models of human neuroblastoma and melanoma, which better reflect the tumor behavior in patients, are required to evaluate the effectiveness of the various targeted liposomal formulations and their possible systemic and organ-specific toxicity. The most multifunctional targeted liposomes are herein described, with primary attention on testing their efficacy in clinically relevant animal models for the treatment of neuroblastoma and melanoma.
Insights
Targeted liposomes offer a promising approach for treating neuroblastoma and melanoma by improving drug delivery and reducing toxicity. Multifunctional liposomes are being tested in animal models to enhance therapeutic efficacy for these difficult-to-treat cancers.
Area of Science:
- Oncology
- Nanotechnology
- Pharmacology
Background:
- Neuroblastoma and melanoma are aggressive cancers with poor prognoses due to treatment resistance.
- Current therapies are limited by poor drug delivery and significant systemic toxicity.
- Targeted cancer therapy, particularly using liposomes, shows potential to overcome these limitations.
Purpose of the Study:
- To explore the potential of multifunctional targeted liposomes for treating neuroectodermal tumors.
- To evaluate the efficacy and toxicity of liposomal drug delivery systems in preclinical models.
- To advance novel therapeutic strategies for neuroblastoma and melanoma.
Main Methods:
- Utilizing sterically stabilized liposomes for enhanced drug delivery to tumor sites.
- Investigating the targeting of tumor-associated antigens and genes.
- Employing clinically relevant animal models of human neuroblastoma and melanoma for efficacy testing.
Main Results:
- Liposomal encapsulation improves drug delivery and reduces toxicity compared to conventional methods.
- Targeted liposomes demonstrate selective localization to solid tumors.
- Multifunctional liposomes show promise in preclinical studies for combined targeting of cancer cells and vasculature.
Conclusions:
- Targeted liposomal formulations represent a promising strategy for improving the treatment of neuroblastoma and melanoma.
- Further evaluation in relevant animal models is crucial to assess the therapeutic potential and safety of these novel drug delivery systems.
- Multifunctional liposomes offer a pathway for developing more effective and selective cancer therapies.
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