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Updated: Jul 3, 2026

Ex Vivo Expansion of Hematopoietic Stem Cells from Human Umbilical Cord Blood-derived CD34+ Cells Using Valproic Acid
Published on: April 11, 2019
High incidence of vaproate-induced coagulation disorders in children receiving valproic acid: a prospective study
Stephan Koenig1, Thorsten Gerstner, Anja Keller
1Department of Pediatrics, Germany, Mannheim University Hospital, University of Heidelberg, Germany. drstkoenig@aol.com
Insights
Valproate therapy commonly causes blood coagulation disturbances in children, including acquired von Willebrand
Area of Science:
- Pharmacology and Toxicology
- Hematology
- Pediatrics
Background:
- Valproate is a widely used antiepileptic drug.
- Previous reports suggest valproate may affect blood coagulation.
- The clinical significance of these potential disturbances requires further investigation.
Purpose of the Study:
- To prospectively evaluate the incidence and nature of blood coagulation disturbances in children newly treated with valproate.
- To assess changes in various coagulation parameters over time during valproate therapy.
Main Methods:
- Prospective trial involving 23 children newly treated with valproate.
- Blood samples collected at baseline, 6 weeks, >6 weeks, and >6 months of therapy.
- Analysis included platelet counts, von Willebrand factor (vWF) assays, fibrinogen, factor XIII, thrombelastography, and other coagulation tests.
Main Results:
- Significant decreases observed in fibrinogen, prothrombin time, activated partial thromboplastin time, vWF antigen, vWF ristocetin cofactor, and antithrombin III activity.
- 17% of patients developed subnormal factor XIII levels, particularly after 6 months of therapy.
- Acquired von Willebrand's disease developed in six children; thrombocytopenia occurred in 8% but was not statistically significant.
Conclusions:
- Valproate therapy frequently induces blood coagulation disturbances in children, though rarely symptomatic.
- Acquired von Willebrand's disease and hypofibrinogenemia are potential concerns, especially in surgical or trauma settings.
- Factor XIII deficiency is notable and warrants attention in patients on valproate therapy.
Abstract:
Reports have been published on blood coagulation disturbances by valproate therapy. In the present prospective trial, blood samples were drawn before valproate therapy, after 6 weeks of therapy, after more than 6 weeks and after longer than 6 months of valproate therapy from 23 children newly treated with valproate. Two children developed thrombocytopenia, and six children with initial normal von Willebrand factor showed acquired von Willebrand's disease. Fibrinogen levels dropped below the lower limit in 12 patients and subnormal factor XIII plasma levels were observed in 17% of patients. No patient developed signs of hemorrhage. Eight percent of patients developed valproate-induced thrombocytopenia. Reduction in platelets did not reach statistic significance. Thrombelastography showed a 47% incidence of altered platelet function. We found a statistically significant, positive correlation between clotting time of collagen extrinsic pathway inhibitor and, accordingly, adenosindiphosphate and valproate level. Plasmatic coagulation investigations showed a significant decrease of prothrombin time. Activated partial thromboplastin time measurements also showed significant prolongation with valproate. Activity of von Willebrand factor antigen and von Willebrand factor ristocetin cofactor significantly decreased. Factor XIII activity significantly decreased after valproate therapy for longer than 6 months (17% of children). Fibrinogen was significantly reduced. In the coagulatory system a decrease in the main antiprotease antithrombin III activity was observed. Blood coagulation disturbances are common in patients with valproate, but rarely become clinically symptomatic. Acquired von Willebrand's disease and hypofibrinogenemia may become relevant in patients with surgery or trauma. Particular attention should be paid to factor-XIII deficiency, which is especially seen with valproate therapy.
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