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Improved metabolic correction in patients with lysosomal storage disease treated with hematopoietic stem cell

Robert F Wynn1, J Ed Wraith, Jean Mercer

  • 1Department of Haematology and BMT, Royal Manchester Children's Hospital, Manchester, United Kingdom. robert.wynn@cmmc.nhs.uk

The Journal of Pediatrics
|March 28, 2009
PubMed

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