Angiokeratoma regression in a Fabry disease after treatment with agalsidase-beta: clinical effectiveness marker?
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In Vitro Enzyme Measurement to Test Pharmacological Chaperone Responsiveness in Fabry and Pompe Disease
Published on: December 20, 2017
Journal of the European Academy of Dermatology and Venereology : JEADV
|November 21, 2009
Abstract
No abstract available in PubMed .