Related Experiment Video

Updated: Jun 17, 2026

An In Vitro Model for the Study of Cellular Pathophysiology in Globoid Cell Leukodystrophy
07:45

An In Vitro Model for the Study of Cellular Pathophysiology in Globoid Cell Leukodystrophy

Published on: October 21, 2014

Gene therapy in metachromatic leukodystrophy

C Sevin1, N Cartier-Lacave, P Aubourg

  • 1French Institute for Health and Medical Research, Paris Descartes University and Department of Pediatric Neurology, Hôpital Saint-Vincent de Paul, Paris, France.

International Journal of Clinical Pharmacology and Therapeutics
|December 31, 2009
PubMed

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