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Familial growth hormone releasing factor deficiency in pseudopseudohypoparathyroidism

H F Stirling1, D G Barr, C J Kelnar

  • 1Department of Child Life and Health, University of Edinburgh.

Insights

This study reports the first case of growth hormone releasing factor deficiency in pseudopseudohypoparathyroidism. A boy with this condition showed improved growth after hormone treatment.

Area of Science:

  • Endocrinology
  • Genetics
  • Pediatrics

Background:

  • Pseudopseudohypoparathyroidism (PHP) is a genetic disorder characterized by resistance to parathyroid hormone.
  • Growth hormone (GH) deficiency can lead to short stature in children.

Observation:

  • A mother with PHP and her son presented with short stature and poor spontaneous growth hormone secretion.
  • Provocation tests indicated a deficiency in growth hormone releasing factor (GHRF).

Findings:

  • This is the first documented instance of GHRF deficiency associated with PHP.
  • The affected boy demonstrated a positive response to growth hormone (GH) therapy over three years.

Implications:

  • This finding suggests a potential link between GHRF deficiency and PHP.
  • Early diagnosis and GH treatment may improve growth outcomes in affected children.

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