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CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications
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CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications

Published on: August 9, 2022

Current understanding of the Wiskott-Aldrich syndrome and prospects for gene therapy

Sara Trifari1, Francesco Marangoni, Samantha Scaramuzza

  • 1San Raffaele-Telethon Institute for Gene Therapy (HSR-TIGET), Via Olgettina 58, 20132 Milan, Italy. s.trifari@hsr.it

Expert Review of Clinical Immunology
|May 19, 2010
PubMed

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