Platelets as delivery systems for disease treatments

Qizhen Shi1, Robert R Montgomery

  • 1Blood Research Institute, BloodCenter of Wisconsin, Departments of Pediatrics, Medical College of Wisconsin, Children's Hospital of Wisconsin, Milwaukee, USA. qizhen.shi@bcw.edu

Summary

Platelets can be engineered for gene therapy. This review focuses on using platelets to deliver Factor VIII (FVIII) for treating hemophilia A, a bleeding disorder.

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