Inborn Errors of Metabolism
Glucose Transporters
Oligosaccharide Assembly
Genomic Imprinting and Inheritance
Lysosomal Hydrolases
Cell Specific Gene Expression
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In Vitro Enzyme Measurement to Test Pharmacological Chaperone Responsiveness in Fabry and Pompe Disease
Published on: December 20, 2017
Mihir Sarkar1, Some Suvra Bose, Gobinda Mondal
1Department of Pediatrics, Medical College and Hospital, 88, College Street, Kolkata, India. mihir_iway_2005@sify.com
A rare form of galactosemia caused by uridine diphosphate galactose-4-epimerase (GALE) deficiency presented with jaundice and failure to thrive. Dietary changes reversed symptoms, indicating GALE deficiency is treatable.
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