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Evaluation of Exon Inclusion Induced by Splice Switching Antisense Oligonucleotides in SMA Patient Fibroblasts
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Spinal muscular atrophy: a new player joins the battle for SMN2 exon 7 splicing

Simona Pedrotti1, Claudio Sette

  • 1Department of Public Health and Cell Biology, University of Rome Tor Vergata, Laboratory of Neuroembryology at CERC, Fondazione Santa Lucia, Rome, Italy.

Cell Cycle (Georgetown, Tex.)
|October 5, 2010
PubMed

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