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Evaluation of Exon Inclusion Induced by Splice Switching Antisense Oligonucleotides in SMA Patient Fibroblasts
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Potential therapeutic applications of antisense morpholino oligonucleotides in modulation of splicing in primary

Liutao Du1, Richard A Gatti

  • 1Department of Pathology and Laboratory Medicine, The David Geffen School of Medicine at UCLA, CA 90095-1732, USA. Ldu@mednet.ucla.edu

Journal of Immunological Methods
|December 15, 2010
PubMed

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