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Updated: Jun 5, 2026

In Vitro Enzyme Measurement to Test Pharmacological Chaperone Responsiveness in Fabry and Pompe Disease
10:16

In Vitro Enzyme Measurement to Test Pharmacological Chaperone Responsiveness in Fabry and Pompe Disease

Published on: December 20, 2017

[Experience in the management of pediatric patients with Gaucher disease]

María Teresa Pompa-Garza1, María Guadalupe González-Villarreal, José Luis Cedillo-de la Cerda

  • 1Departamento de Hematología Pediátrica, Hospital de Especialidades 25, Instituto Mexicano del Seguro Social, Monterrey, Nuevo León, México. terepompa@yahoo.com.mx

Revista Medica Del Instituto Mexicano Del Seguro Social
|December 28, 2010
PubMed

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