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Clinical trial methodologies for disease-modifying therapeutic approaches
1Department of Neurosciences, University of California San Diego, La Jolla, CA 92093, USA. paisen@ucsd.edu
Neurobiology of Aging
|October 11, 2011
Summary
Alzheimer
Area of Science:
- Neurology
- Biomarker Research
- Clinical Trial Design
Background:
- Alzheimer's disease (AD) research has advanced significantly.
- Biomarker research offers new tools for clinical trials.
Purpose of the Study:
- To highlight the role of biomarkers in Alzheimer's disease research.
- To discuss the utility of biomarkers in improving clinical trial design.
Main Methods:
- Review of recent advances in Alzheimer's disease biomarker research.
- Analysis of biomarker application in patient selection for clinical trials.
Main Results:
- Biomarkers enable the selection of individuals with Alzheimer's disease before dementia onset.
- Neuroimaging biomarkers show promise as trial endpoints for early-stage and asymptomatic disease.
Conclusions:
- Biomarkers are crucial for enhancing Alzheimer's disease clinical trial design.
- Further validation is required for regulatory approval of neuroimaging biomarkers in early-stage trials.
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