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Evaluation of Exon Inclusion Induced by Splice Switching Antisense Oligonucleotides in SMA Patient Fibroblasts
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Antisense oligonucleotides shed new light on the pathogenesis and treatment of spinal muscular atrophy

Jiing-Kuan Yee1, Ren-Jang Lin

  • 1Department of Virology, Beckman Research Institute, City of Hope National Medical Center, Duarte, California 91010, USA. jyee@coh.org

Molecular Therapy : the Journal of the American Society of Gene Therapy
|January 5, 2012
PubMed
Abstract

No abstract available in PubMed .

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