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Novel pharmacological chaperones that correct phenylketonuria in mice

Sandra Santos-Sierra1, Johannes Kirchmair, Anna M Perna

  • 1Sections of Biochemical and Clinical Pharmacology, Department of Medical Genetics, Molecular and Clinical Pharmacology, Innsbruck Medical University, 6020 Innsbruck, Austria.

Human Molecular Genetics
|January 17, 2012
PubMed

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