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CRISPR/Cas9-mediated Targeted Integration In Vivo Using a Homology-mediated End Joining-based Strategy
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Gene therapy for Fanconi anemia: one step closer to the clinic

Jakub Tolar1, Pamela S Becker, D Wade Clapp

  • 1Division of Blood and Marrow Transplantation, University of Minnesota , Minneapolis, MN 55455, USA. tolar003@umn.edu

Human Gene Therapy
|January 18, 2012
PubMed
Abstract

No abstract available in PubMed .

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