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Updated: May 24, 2026

One-step Metabolomics: Carbohydrates, Organic and Amino Acids Quantified in a Single Procedure
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Gene therapy for metabolic disorders: an overview with a focus on urea cycle disorders

Ian E Alexander1, Cindy Kok, Allison P Dane

  • 1Gene Therapy Research Unit, Children's Medical Research Institute and The Children's Hospital at Westmead, Locked Bag 4001, Westmead, NSW, 2145, Australia. ian.alexander@health.nsw.gov.au

Journal of Inherited Metabolic Disease
|March 10, 2012
PubMed

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