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Gene therapy approaches for lysosomal storage disorders, a good model for the treatment of mendelian diseases

Rosella Tomanin1, Alessandra Zanetti, Eva Zaccariotto

  • 1Gene Therapy Laboratory, Department of Pediatrics, University of Padova, Italy.

Acta Paediatrica (Oslo, Norway : 1992)
|March 21, 2012
PubMed
Abstract

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