Related Experiment Video

Updated: May 23, 2026

An In Vitro Model for the Study of Cellular Pathophysiology in Globoid Cell Leukodystrophy
07:45

An In Vitro Model for the Study of Cellular Pathophysiology in Globoid Cell Leukodystrophy

Published on: October 21, 2014

Failure of repeated cyclophosphamide pulse therapy in childhood cerebral X-linked adrenoleukodystrophy

Gabriella Ana Horvath1, Florian Eichler, Ken Poskitt

  • 1Department of Biochemical Diseases, British Columbia Children's Hospital, Vancouver, British Columbia, Canada. ghorvath@cw.bc.ca

Neuropediatrics
|March 21, 2012
PubMed

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