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Thalassemia

Yesim Aydinok1

  • 1Ege University Children's Hospital, Department of Pediatric Hematology, Ege University Hospital Blood Bank, 35100 Bornova, Izmir, Turkey. yesim.aydinok@ege.edu.tr

Hematology (Amsterdam, Netherlands)
|April 18, 2012
PubMed
Summary

Beta-thalassemia major is a common inherited anemia affecting 60,000 infants globally each year. Current management relies on blood transfusions and iron chelation, despite advances in gene therapy.

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