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Fabry disease in children: agalsidase-beta enzyme replacement therapy

L Borgwardt1, U Feldt-Rasmussen, A K Rasmussen

  • 1Department of Clinical Genetics, Centre for Inherited Metabolic Disorders, Copenhagen University Hospital, Rigshospitalet, Copenhagen, Denmark. Line.gutte.borgwardt@rh.regionh.dk

Clinical Genetics
|August 14, 2012
PubMed

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