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CRISPR/Cas9-mediated Targeted Integration In Vivo Using a Homology-mediated End Joining-based Strategy
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Towards germline gene therapy of inherited mitochondrial diseases

Masahito Tachibana1, Paula Amato, Michelle Sparman

  • 1Division of Reproductive & Developmental Sciences, Oregon National Primate Research Center, Oregon Health & Science University, 505 NW 185th Avenue, Beaverton, Oregon 97006, USA.

Nature
|October 30, 2012
PubMed

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