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Constitutive and Inducible Systems for Genetic In Vivo Modification of Mouse Hepatocytes Using Hydrodynamic Tail Vein Injection
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Deep intronic 'mutations' cause hemophilia A: application of next generation sequencing in patients without

B Pezeshkpoor1, N Zimmer, N Marquardt

  • 1Institute of Experimental Hematology and Transfusion Medicine, University of Bonn, Bonn, Germany.

Journal of Thrombosis and Haemostasis : JTH
|July 2, 2013
PubMed
Abstract

Keywords:
factor VIIIhemophilia AintronsmRNAmutations

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