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Published on: September 1, 2015
Polycystic kidney disease: a case of suppressed autophagy?
Kameswaran Ravichandran1, Charles L Edelstein1
1Division of Renal Diseases and Hypertension, University of Colorado at Denver, Aurora, CO.
Abstract:
Autosomal-dominant polycystic kidney disease is the most common form of polycystic kidney disease in adults and is caused by a mutation in the polycystic kidney disease 1 or 2 genes, which encode, respectively, polycystin-1 and polycystin-2. Autophagy is present in polycystic kidneys in rat and mouse models of polycystic kidney disease. Autophagy has yet to be shown in human polycystic kidney disease kidneys. The mechanism of cyst growth has been studied extensively in vitro and in vivo. Multiple molecules and signaling pathways have been implicated in cyst growth including mammalian target of rapamycin, the renin-angiotensin-aldosterone system, vasopressin and cyclic adenosine monophosphate, epidermal growth factor and insulin-like growth factor tyrosine kinases, vascular endothelial growth factor, extracellular signal-related kinase, tumor necrosis factor-α, cyclin-dependent kinases, caspases and apoptosis, and cyclic adenosine monophosphate-activated protein kinases. Many of the agents that inhibit these signaling pathways and slow cyst growth are also autophagy inducers such as mammalian target of rapamycin inhibitors, cyclin-dependent kinase inhibitors, caspase inhibitors, tyrosine kinase inhibitors, metformin, curcumin, and triptolide. There are reasons to believe that suppression of autophagy may play a role in cyst formation and growth. This review presents the hypothesis that suppression of autophagy may play a role in cyst formation and growth, based on the following: (1) many of the agents that protect against polycystic kidney disease also induce autophagy, (2) suppression of autophagy in polycystic kidney disease 1 knockout cells, (3) a defect in autophagy in congenital polycystic kidney mice with polycystic kidney disease, (4) how suppressed autophagy may relate to apoptosis in polycystic kidney disease, and (5) conditions with defective cilia, the ciliopathies, are associated with decreased autophagy.
Insights
Suppressed autophagy may contribute to cyst formation in autosomal-dominant polycystic kidney disease. Treatments that induce autophagy show promise in slowing cyst growth and protecting against this common genetic kidney disorder.
Area of Science:
- Nephrology
- Cell Biology
- Genetics
Background:
- Autosomal-dominant polycystic kidney disease (ADPKD) is a common genetic disorder caused by mutations in PKD1 or PKD2 genes.
- Autophagy, a cellular degradation process, is observed in animal models of ADPKD but not yet confirmed in human ADPKD kidneys.
- Cyst formation and growth in ADPKD involve numerous signaling pathways and molecules.
Purpose of the Study:
- To review the evidence suggesting a role for autophagy suppression in the pathogenesis of ADPKD.
- To explore the connection between autophagy, cystogenesis, and potential therapeutic targets in ADPKD.
Main Methods:
- Review of existing literature on ADPKD mechanisms, autophagy, and therapeutic agents.
- Analysis of data from in vitro and in vivo studies, including animal models and cell lines.
- Examination of signaling pathways implicated in cyst growth and their relationship with autophagy.
Main Results:
- Many agents that inhibit ADPKD cyst growth are also inducers of autophagy.
- Evidence suggests autophagy suppression in PKD1 knockout cells and in congenital polycystic kidney mice.
- Connections are drawn between suppressed autophagy, apoptosis, and ciliopathies in the context of ADPKD.
Conclusions:
- Suppression of autophagy is hypothesized to play a significant role in the formation and growth of cysts in ADPKD.
- Targeting autophagy induction presents a potential therapeutic strategy for managing ADPKD.
- Further research is needed to confirm the role of autophagy in human ADPKD and its therapeutic implications.
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