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Gene therapy for hemoglobinopathies: the state of the field and the future

Shanmuganathan Chandrakasan1, Punam Malik2

  • 1Division of Hematology, Oncology and Bone Marrow Transplant, Cancer and Blood Disease Institute (CBDI), Cincinnati Children's Hospital Medical Center (CCHMC), 3333 Burnet Avenue, Cincinnati, OH 45229, USA.

Hematology/Oncology Clinics of North America
|March 5, 2014
PubMed

Keywords:
Gene therapyHemoglobinopathySickle cell diseaseThalassemia

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