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Gene therapy for Wiskott-Aldrich syndrome--long-term efficacy and genotoxicity

Christian Jörg Braun1, Kaan Boztug, Anna Paruzynski

  • 1Dr. von Hauner Children's Hospital, Ludwig Maximilians University Munich, 80337 Munich, Germany.

Science Translational Medicine
|March 14, 2014
PubMed

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