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Long-term effectiveness of enzyme replacement therapy in Fabry disease: results from the NCS-LSD cohort study

L J Anderson1, K M Wyatt, W Henley

  • 1Institute of Health Research, University of Exeter Medical School, Veysey Building, Salmon Pool Lane, Exeter, Devon, UK, EX2 4SG.

Journal of Inherited Metabolic Disease
|May 17, 2014
PubMed
Abstract

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