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Splicing-correcting therapeutic approaches for retinal dystrophies: where endogenous gene regulation and specificity

Niccolò Bacchi1, Simona Casarosa2, Michela A Denti3

  • 1Centre for Integrative Biology (CIBIO) - University of Trento, Trento, Italy.

Investigative Ophthalmology & Visual Science
|May 29, 2014
PubMed

Keywords:
antisense oligonucleotidesgene therapyretinal dystrophysplicing correction

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