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Lifetime risk estimators in epidemiological studies of Krabbe Disease: Review and Monte Carlo comparison

Alexander H Foss1, Patricia K Duffner2, Randy L Carter1

  • 1Department of Biostatistics; Population Health Observatory; School of Public Health and Health Professions; University at Buffalo; State University of New York; Buffalo, NY USA.

Rare Diseases (Austin, Tex.)
|July 9, 2014
PubMed

Keywords:
Monte Carlo methodepidemiologygloboid cellinborn errorsincidenceleukodystrophylifetime risklysosomal storage diseasesmetabolismprevalence

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