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Updated: Apr 26, 2026

Forskolin-induced Swelling in Intestinal Organoids: An In Vitro Assay for Assessing Drug Response in Cystic Fibrosis Patients
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CFTR potentiators: not an open and shut case

John P Clancy1

  • 1Cincinnati Children's Hospital Medical Center and the University of Cincinnati, Cincinnati, OH 45229, USA.

Science Translational Medicine
|August 8, 2014
PubMed
Summary

New cystic fibrosis (CF) drug insights reveal both benefits and drawbacks, prompting a reevaluation of therapeutic discovery and development strategies for CF patients with common mutations.

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