Emerging treatments for amyloidosis

Rabya H Sayed1, Philip N Hawkins2, Helen J Lachmann1

  • 11] National Amyloidosis Centre, UCL Medical School, Royal Free Hospital, London, UK [2] UCL Centre for Nephrology, UCL Medical School, Royal Free Hospital, London, UK.

Kidney International
|December 4, 2014
PubMed
Summary

New targeted therapies are emerging for amyloidosis, a disease caused by protein misfolding that can lead to organ failure. These novel treatments, including protein stabilizers and immunotherapy, are now in clinical trials.

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