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Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
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Adeno-associated virus-mediated microRNA delivery and therapeutics

Jun Xie1, Daniel Robert Burt1, Guangping Gao1

  • 1Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts.

Seminars in Liver Disease
|January 31, 2015
PubMed

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