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Profiling Sensitivity to Targeted Therapies in EGFR-Mutant NSCLC Patient-Derived Organoids
Published on: November 22, 2021
The changing world of oncology drug development-A global pharmaceutical company's perspective
1Oncology Innovative Medicines Unit, AstraZeneca, Macclesfield, UK. susan.galbraith@astrazeneca.com.
Abstract:
Recent approvals for oncology drugs have seen an increasing proportion directed to specific genetic targets identified with an associated companion diagnostic test. In addition, there is a wave of drugs directed against immune 'checkpoints' which promise to transform the way cancer is treated in the next decade. We can increase the probability of success in drug development based on a thorough mechanistic understanding of how a target drug affects cancer biology and the specific biological and genotypic context in which it operates. This article compares and contrasts the discovery and development of gefitinib-the first EGFR tyrosine kinase inhibitor and AZD9291, an irreversible inhibitor of both sensitizing and resistant mutated EGFR. This demonstrates how the better understanding we now have of the genetic changes driving the cancer growth and the biochemical structure and function of the mutated proteins, has led to a much faster developmental path with higher likelihood of success in pivotal trials. An emerging trend in response to the challenge of the increasing segmentation of cancers based on their genetic makeup is the development of 'basket' studies which include one or more screening tests for multiple genetic aberrations and the direction of patients to one of several arms of a clinical trial based on the specific aberration in their tumor. In the face of both the wealth of genetic information about cancer and the challenges of drug development, collaboration across academia and industry is vital. There is great potential to benefit from more 'open innovation' to address some of these challenges and opportunities. Far from there being a decline in innovation in pharmaceutical development, I see that we are in one of the most exciting times in cancer drug development with innovation in every aspect of how we discover and develop new therapies.
Insights
Advancements in cancer drug development, including targeted therapies and immune checkpoint inhibitors, are transforming treatment. A deeper understanding of cancer genetics and protein function accelerates drug discovery and increases success rates.
Area of Science:
- Oncology
- Pharmacology
- Genetics
Background:
- Oncology drug approvals increasingly target specific genetic mutations with companion diagnostics.
- Immune checkpoint inhibitors represent a significant advancement in cancer treatment strategies.
- Mechanistic understanding of drug action in specific cancer contexts improves development success.
Purpose of the Study:
- Compare and contrast the development of gefitinib and AZD9291, focusing on EGFR inhibitors.
- Illustrate how improved understanding of cancer genetics and protein function accelerates drug development.
- Highlight emerging trends like basket studies in cancer clinical trials.
Main Methods:
- Comparative analysis of gefitinib and AZD9291 discovery and development pathways.
- Review of mechanistic insights into EGFR mutations and inhibitor actions.
- Examination of the role of genetic profiling in modern clinical trial design, including basket studies.
Main Results:
- Enhanced understanding of cancer genetics and mutated protein function has expedited drug development for targeted therapies like EGFR inhibitors.
- The development path for AZD9291, an irreversible EGFR inhibitor, was significantly faster and more successful than earlier agents due to improved knowledge.
- Basket studies are emerging as a key strategy to address cancer's genetic heterogeneity and streamline clinical trials.
Conclusions:
- Improved understanding of cancer biology and genetics is crucial for successful drug development.
- Targeted therapies and immune checkpoint inhibitors are revolutionizing oncology.
- Collaboration and open innovation are vital for navigating the complexities of modern cancer drug discovery and development.
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